Int J Environ Res Public Health. 2023 Aug 3;20(15):6516. doi: 10.3390/ijerph20156516.
PMID:37569056
Diffusing Capacity of the Lungs for Carbon Monoxide and Echocardiographic Parameters in Identifying Mild Pulmonary Hypertension in the EUSTAR Cohort of Patients With Systemic Sclerosis.
Colalillo A, Hachulla E, Pellicano C, Smith V, Bergmann C, Riemekasten G, Zanatta E, Henes J, Launay D, Marcoccia A, Gheorghiu AM, Truchetet ME, Iannone F, Simeón Aznar CP, Oliveira S, Vonk M, Del Galdo F, Rosato E; EUSTAR Collaborators.
Chest. 2024 Oct;166(4):837-844. doi: 10.1016/j.chest.2024.05.010. Epub 2024 Jun 6.
A randomized, placebo-controlled clinical trial evaluating olipudase alfa enzyme replacement therapy for chronic acid sphingomyelinase deficiency (ASMD) in adults: One-year results.
Wasserstein M, Lachmann R, Hollak C, Arash-Kaps L, Barbato A, Gallagher RC, Giugliani R, Guelbert NB, Ikezoe T, Lidove O, Mabe P, Mengel E, Scarpa M, Senates E, Tchan M, Villarrubia J, Chen Y, Furey S, Thurberg BL, Zaher A, Kumar M.