A randomized, placebo-controlled clinical trial evaluating olipudase alfa enzyme replacement therapy for chronic acid sphingomyelinase deficiency (ASMD) in adults: One-year results.
Wasserstein M, Lachmann R, Hollak C, Arash-Kaps L, Barbato A, Gallagher RC, Giugliani R, Guelbert NB, Ikezoe T, Lidove O, Mabe P, Mengel E, Scarpa M, Senates E, Tchan M, Villarrubia J, Chen Y, Furey S, Thurberg BL, Zaher A, Kumar M.
Diffusing Capacity of the Lungs for Carbon Monoxide and Echocardiographic Parameters in Identifying Mild Pulmonary Hypertension in the EUSTAR Cohort of Patients With Systemic Sclerosis.
Colalillo A, Hachulla E, Pellicano C, Smith V, Bergmann C, Riemekasten G, Zanatta E, Henes J, Launay D, Marcoccia A, Gheorghiu AM, Truchetet ME, Iannone F, Simeón Aznar CP, Oliveira S, Vonk M, Del Galdo F, Rosato E; EUSTAR Collaborators.
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PMID:38849072
Diffusing Capacity of Carbon Monoxide in Assessment of COPD.
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