CRISPR/Cas9 beta-globin gene targeting in human haematopoietic stem cells.
Dever DP, Bak RO, Reinisch A, Camarena J, Washington G, Nicolas CE, Pavel-Dinu M, Saxena N, Wilkens AB, Mantri S, Uchida N, Hendel A, Narla A, Majeti R, Weinberg KI, Porteus MH.
Nature. 2016 Nov 17;539(7629):384-389. doi: 10.1038/nature20134. Epub 2016 Nov 7.
Guidelines for the use and interpretation of assays for monitoring autophagy (3rd edition).
Klionsky DJ, Abdelmohsen K, Abe A, Abedin MJ, Abeliovich H, Acevedo Arozena A, Adachi H, Adams CM, Adams PD, Adeli K, Adhihetty PJ, Adler SG, Agam G, Agarwal R, Aghi MK, Agnello M, Agostinis P, Aguilar PV, Aguirre-Ghiso J, Airoldi EM, Ait-Si-Ali S, Akematsu T, Akporiaye ET, Al-Rubeai M, Albaiceta GM, Albanese C, Albani D, Albert ML, Aldudo J, Algül H, Alirezaei M, Alloza I, Almasan A, Almonte-Beceril M, Alnemri ES, Alonso C, Altan-Bonnet N, Altieri DC, Alvarez S, Alvarez-Erviti L, Alves S, Amadoro G, Amano A, Amantini C, Ambrosio S, Amelio I, Amer AO, Amessou M, Amon A, An Z, Anania FA, Andersen SU, Andley UP, Andreadi CK, Andrieu-Abadie N, Anel A, Ann DK, Anoopkumar-Dukie S, Antonioli M, Aoki H, Apostolova N, Aquila S, Aquilano K, Araki K, Arama E, Aranda A, Araya J, Arcaro A, Arias E, Arimoto H, Ariosa AR, Armstrong JL, Arnould T, Arsov I, Asanuma K, Askanas V, Asselin E, Atarashi R, Atherton SS, Atkin JD, Attardi LD, Auberger P, Auburger G, Aurelian L, Autelli R, Avagliano L, Avantaggiati ML, Avrahami L, Awale S, Azad N, Bachetti T, Backer JM, Bae DH, Bae JS, Bae ON, Bae SH, Baehrecke EH, Baek SH, Baghdiguian S, Bagniewska-Zadworna A, Bai H, Bai J, Bai XY, Bailly Y, Balaji KN, …
Autophagy. 2016;12(1):1-222. doi: 10.1080/15548627.2015.1100356.
Robust CAR-T memory formation and function via hematopoietic stem cell delivery.
Zhen A, Carrillo MA, Mu W, Rezek V, Martin H, Hamid P, Chen ISY, Yang OO, Zack JA, Kitchen SG.
PLoS Pathog. 2021 Apr 1;17(4):e1009404. doi: 10.1371/journal.ppat.1009404. eCollection 2021 Apr.
CRISPR/Cas9-mediated gene editing. A promising strategy in hematological disorders.
Ugalde L, Fañanas S, Torres R, Quintana-Bustamante O, Río P.
Cytotherapy. 2023 Mar;25(3):277-285. doi: 10.1016/j.jcyt.2022.11.014. Epub 2023 Jan 5.
Antibody based conditioning for allogeneic hematopoietic stem cell transplantation.
Saha A, Blazar BR.
Front Immunol. 2022 Oct 20;13:1031334. doi: 10.3389/fimmu.2022.1031334. eCollection 2022.
Optimal Delivery of Follow-Up Care After Allogeneic Hematopoietic Stem-Cell Transplant: Improving Patient Outcomes with a Multidisciplinary Approach.
Giaccone L, Felicetti F, Butera S, Faraci D, Cerrano M, Dionisi Vici M, Brunello L, Fortunati N, Brignardello E, Bruno B.
J Blood Med. 2020 May 15;11:141-162. doi: 10.2147/JBM.S206027. eCollection 2020.
CD47 peptide-cloaked lipid nanoparticles promote cell-specific mRNA delivery.
Papp TE, Zeng J, Shahnawaz H, Akyianu A, Breda L, Yadegari A, Steward J, Shi R, Li Q, Mui BL, Tam YK, Weissman D, Rivella S, Shuvaev V, Muzykantov VR, Parhiz H.
Mol Ther. 2025 Mar 13:S1525-0016(25)00192-3. doi: 10.1016/j.ymthe.2025.03.018. Online ahead of print.
Novel approaches and mechanisms in hematopoietic stem cell gene therapy.
Bigger BW, Wynn RF.
Discov Med. 2014 Apr;17(94):207-15.
Core-shell nanotherapeutics with leukocyte membrane camouflage for biomedical applications.
Fan M, Jiang M.
J Drug Target. 2020 Nov;28(9):873-881. doi: 10.1080/1061186X.2020.1757102. Epub 2020 Apr 24.
Bioinspired and Biomimetic Nanomedicines.
Chen Z, Wang Z, Gu Z.
Acc Chem Res. 2019 May 21;52(5):1255-1264. doi: 10.1021/acs.accounts.9b00079. Epub 2019 Apr 12.
