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delivery combined with blood and hematopoietic disease相关文献:
CRISPR/Cas9 beta-globin gene targeting in human haematopoietic stem cells.
Dever DP, Bak RO, Reinisch A, Camarena J, Washington G, Nicolas CE, Pavel-Dinu M, Saxena N, Wilkens AB, Mantri S, Uchida N, Hendel A, Narla A, Majeti R, Weinberg KI, Porteus MH.
Nature. 2016 Nov 17;539(7629):384-389. doi: 10.1038/nature20134. Epub 2016 Nov 7.
PMID:27820943
CD47 peptide-cloaked lipid nanoparticles promote cell-specific mRNA delivery.
Papp TE, Zeng J, Shahnawaz H, Akyianu A, Breda L, Yadegari A, Steward J, Shi R, Li Q, Mui BL, Tam YK, Weissman D, Rivella S, Shuvaev V, Muzykantov VR, Parhiz H.
Mol Ther. 2025 Jul 2;33(7):3195-3208. doi: 10.1016/j.ymthe.2025.03.018. Epub 2025 Mar 13.
PMID:40087866
Guidelines for the use and interpretation of assays for monitoring autophagy (3rd edition).
Klionsky DJ, Abdelmohsen K, Abe A, Abedin MJ, Abeliovich H, Acevedo Arozena A, Adachi H, Adams CM, Adams PD, Adeli K, Adhihetty PJ, Adler SG, Agam G, Agarwal R, Aghi MK, Agnello M, Agostinis P, Aguilar PV, Aguirre-Ghiso J, Airoldi EM, Ait-Si-Ali S, Akematsu T, Akporiaye ET, Al-Rubeai M, Albaiceta GM, Albanese C, Albani D, Albert ML, Aldudo J, Algül H, Alirezaei M, Alloza I, Almasan A, Almonte-Beceril M, Alnemri ES, Alonso C, Altan-Bonnet N, Altieri DC, Alvarez S, Alvarez-Erviti L, Alves S, Amadoro G, Amano A, Amantini C, Ambrosio S, Amelio I, Amer AO, Amessou M, Amon A, An Z, Anania FA, Andersen SU, Andley UP, Andreadi CK, Andrieu-Abadie N, Anel A, Ann DK, Anoopkumar-Dukie S, Antonioli M, Aoki H, Apostolova N, Aquila S, Aquilano K, Araki K, Arama E, Aranda A, Araya J, Arcaro A, Arias E, Arimoto H, Ariosa AR, Armstrong JL, Arnould T, Arsov I, Asanuma K, Askanas V, Asselin E, Atarashi R, Atherton SS, Atkin JD, Attardi LD, Auberger P, Auburger G, Aurelian L, Autelli R, Avagliano L, Avantaggiati ML, Avrahami L, Awale S, Azad N, Bachetti T, Backer JM, Bae DH, Bae JS, Bae ON, Bae SH, Baehrecke EH, Baek SH, Baghdiguian S, Bagniewska-Zadworna A, Bai H, Bai J, Bai XY, Bailly Y, Balaji KN, …
Autophagy. 2016;12(1):1-222. doi: 10.1080/15548627.2015.1100356.
PMID:26799652
Bioinspired and Biomimetic Nanomedicines.
Chen Z, Wang Z, Gu Z.
Acc Chem Res. 2019 May 21;52(5):1255-1264. doi: 10.1021/acs.accounts.9b00079. Epub 2019 Apr 12.
PMID:30977635
CRISPR/Cas9-mediated gene editing. A promising strategy in hematological disorders.
Ugalde L, Fañanas S, Torres R, Quintana-Bustamante O, Río P.
Cytotherapy. 2023 Mar;25(3):277-285. doi: 10.1016/j.jcyt.2022.11.014. Epub 2023 Jan 5.
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Robust CAR-T memory formation and function via hematopoietic stem cell delivery.
Zhen A, Carrillo MA, Mu W, Rezek V, Martin H, Hamid P, Chen ISY, Yang OO, Zack JA, Kitchen SG.
PLoS Pathog. 2021 Apr 1;17(4):e1009404. doi: 10.1371/journal.ppat.1009404. eCollection 2021 Apr.
PMID:33793675
Persistent problems of neutropenia and thrombocytopenia with peripheral blood stem cell transplantation.
Spitzer G, Adkins DR.
J Hematother. 1994 Fall;3(3):193-8. doi: 10.1089/scd.1.1994.3.193.
PMID:7530134
Antibody based conditioning for allogeneic hematopoietic stem cell transplantation.
Saha A, Blazar BR.
Front Immunol. 2022 Oct 20;13:1031334. doi: 10.3389/fimmu.2022.1031334. eCollection 2022.
PMID:36341432
Monocyte/Macrophage-Mediated Transport of Dual-Drug ZIF Nanoplatforms Synergized with Programmed Cell Death Protein-1 Inhibitor Against Microsatellite-Stable Colorectal Cancer.
Ye X, Liu Y, Wei L, Sun Y, Zhang X, Wang H, Guo H, Qin X, Li X, Qu D, Huo J, Chen Y.
Adv Sci (Weinh). 2024 Oct;11(38):e2405886. doi: 10.1002/advs.202405886. Epub 2024 Aug 5.
PMID:39101234
Targeted therapy for leukemia based on nanomaterials.
Qian S, Zheng C, Wu Y, Huang H, Wu G, Zhang J.
Heliyon. 2024 Jul 21;10(15):e34951. doi: 10.1016/j.heliyon.2024.e34951. eCollection 2024 Aug 15.
PMID:39144922
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