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delivery combined with blood and hematopoietic disease相关文献:
CRISPR/Cas9 beta-globin gene targeting in human haematopoietic stem cells.
Dever DP, Bak RO, Reinisch A, Camarena J, Washington G, Nicolas CE, Pavel-Dinu M, Saxena N, Wilkens AB, Mantri S, Uchida N, Hendel A, Narla A, Majeti R, Weinberg KI, Porteus MH.
Nature. 2016 Nov 17;539(7629):384-389. doi: 10.1038/nature20134. Epub 2016 Nov 7.
PMID:27820943
CD47 peptide-cloaked lipid nanoparticles promote cell-specific mRNA delivery.
Papp TE, Zeng J, Shahnawaz H, Akyianu A, Breda L, Yadegari A, Steward J, Shi R, Li Q, Mui BL, Tam YK, Weissman D, Rivella S, Shuvaev V, Muzykantov VR, Parhiz H.
Mol Ther. 2025 Jul 2;33(7):3195-3208. doi: 10.1016/j.ymthe.2025.03.018. Epub 2025 Mar 13.
PMID:40087866
Guidelines for the use and interpretation of assays for monitoring autophagy (3rd edition).
Klionsky DJ, Abdelmohsen K, Abe A, Abedin MJ, Abeliovich H, Acevedo Arozena A, Adachi H, Adams CM, Adams PD, Adeli K, Adhihetty PJ, Adler SG, Agam G, Agarwal R, Aghi MK, Agnello M, Agostinis P, Aguilar PV, Aguirre-Ghiso J, Airoldi EM, Ait-Si-Ali S, Akematsu T, Akporiaye ET, Al-Rubeai M, Albaiceta GM, Albanese C, Albani D, Albert ML, Aldudo J, Algül H, Alirezaei M, Alloza I, Almasan A, Almonte-Beceril M, Alnemri ES, Alonso C, Altan-Bonnet N, Altieri DC, Alvarez S, Alvarez-Erviti L, Alves S, Amadoro G, Amano A, Amantini C, Ambrosio S, Amelio I, Amer AO, Amessou M, Amon A, An Z, Anania FA, Andersen SU, Andley UP, Andreadi CK, Andrieu-Abadie N, Anel A, Ann DK, Anoopkumar-Dukie S, Antonioli M, Aoki H, Apostolova N, Aquila S, Aquilano K, Araki K, Arama E, Aranda A, Araya J, Arcaro A, Arias E, Arimoto H, Ariosa AR, Armstrong JL, Arnould T, Arsov I, Asanuma K, Askanas V, Asselin E, Atarashi R, Atherton SS, Atkin JD, Attardi LD, Auberger P, Auburger G, Aurelian L, Autelli R, Avagliano L, Avantaggiati ML, Avrahami L, Awale S, Azad N, Bachetti T, Backer JM, Bae DH, Bae JS, Bae ON, Bae SH, Baehrecke EH, Baek SH, Baghdiguian S, Bagniewska-Zadworna A, Bai H, Bai J, Bai XY, Bailly Y, Balaji KN, …
Autophagy. 2016;12(1):1-222. doi: 10.1080/15548627.2015.1100356.
PMID:26799652
Bioinspired and Biomimetic Nanomedicines.
Chen Z, Wang Z, Gu Z.
Acc Chem Res. 2019 May 21;52(5):1255-1264. doi: 10.1021/acs.accounts.9b00079. Epub 2019 Apr 12.
PMID:30977635
CRISPR/Cas9-mediated gene editing. A promising strategy in hematological disorders.
Ugalde L, Fañanas S, Torres R, Quintana-Bustamante O, Río P.
Cytotherapy. 2023 Mar;25(3):277-285. doi: 10.1016/j.jcyt.2022.11.014. Epub 2023 Jan 5.
PMID:36610813
Antibody based conditioning for allogeneic hematopoietic stem cell transplantation.
Saha A, Blazar BR.
Front Immunol. 2022 Oct 20;13:1031334. doi: 10.3389/fimmu.2022.1031334. eCollection 2022.
PMID:36341432
Proteasome inhibition enhances oncolytic reovirus therapy in multiple myeloma independently of its direct cytotoxic effects.
Dona AA, Tandoh T, Nigam L, Singer M, Caserta E, Murtadha M, Zhu Y, Moloudizargari M, Sharma P, Napolitano O, Winchester J, Chowdhury A, Pozhitkov A, Sanchez JF, Vahed H, Marcucci G, Coffey M, Nuovo G, Sborov DW, Pichiorri F, Hofmeister CC.
J Hematol Oncol. 2025 Jan 20;18(1):1. doi: 10.1186/s13045-024-01645-3.
PMID:39828738
Monocyte/Macrophage-Mediated Transport of Dual-Drug ZIF Nanoplatforms Synergized with Programmed Cell Death Protein-1 Inhibitor Against Microsatellite-Stable Colorectal Cancer.
Ye X, Liu Y, Wei L, Sun Y, Zhang X, Wang H, Guo H, Qin X, Li X, Qu D, Huo J, Chen Y.
Adv Sci (Weinh). 2024 Oct;11(38):e2405886. doi: 10.1002/advs.202405886. Epub 2024 Aug 5.
PMID:39101234
Core-shell nanotherapeutics with leukocyte membrane camouflage for biomedical applications.
Fan M, Jiang M.
J Drug Target. 2020 Nov;28(9):873-881. doi: 10.1080/1061186X.2020.1757102. Epub 2020 Apr 24.
PMID:32298153
Novel approaches and mechanisms in hematopoietic stem cell gene therapy.
Bigger BW, Wynn RF.
Discov Med. 2014 Apr;17(94):207-15.
PMID:24759625
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