Arch Iran Med. 2021 Dec 1;24(12):919-920. doi: 10.34172/aim.2021.138.
PMID:35014241
Elesclomol alleviates Menkes pathology and mortality by escorting Cu to cuproenzymes in mice.
Guthrie LM, Soma S, Yuan S, Silva A, Zulkifli M, Snavely TC, Greene HF, Nunez E, Lynch B, De Ville C, Shanbhag V, Lopez FR, Acharya A, Petris MJ, Kim BE, Gohil VM, Sacchettini JC.
Science. 2020 May 8;368(6491):620-625. doi: 10.1126/science.aaz8899.
PMID:32381719
Menkes disease.
Kaler SG.
Adv Pediatr. 1994;41:263-304.
PMID:7992686
Menkes disease.
Bankier A.
J Med Genet. 1995 Mar;32(3):213-5. doi: 10.1136/jmg.32.3.213.