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Lethal immunotoxicity in high-dose systemic AAV therapy.
Duan D.
Mol Ther. 2023 Nov 1;31(11):3123-3126. doi: 10.1016/j.ymthe.2023.10.015. Epub 2023 Oct 10.
PMID:37822079
In Vivo Target Gene Activation via CRISPR/Cas9-Mediated Trans-epigenetic Modulation.
Liao HK, Hatanaka F, Araoka T, Reddy P, Wu MZ, Sui Y, Yamauchi T, Sakurai M, O'Keefe DD, Núñez-Delicado E, Guillen P, Campistol JM, Wu CJ, Lu LF, Esteban CR, Izpisua Belmonte JC.
Cell. 2017 Dec 14;171(7):1495-1507.e15. doi: 10.1016/j.cell.2017.10.025. Epub 2017 Dec 7.
PMID:29224783
Cellular interplay in skeletal muscle regeneration and wasting: insights from animal models.
Henrot P, Blervaque L, Dupin I, Zysman M, Esteves P, Gouzi F, Hayot M, Pomiès P, Berger P.
J Cachexia Sarcopenia Muscle. 2023 Apr;14(2):745-757. doi: 10.1002/jcsm.13103. Epub 2023 Feb 21.
PMID:36811134
The endothelial Dll4-muscular Notch2 axis regulates skeletal muscle mass.
Fujimaki S, Matsumoto T, Muramatsu M, Nagahisa H, Horii N, Seko D, Masuda S, Wang X, Asakura Y, Takahashi Y, Miyamoto Y, Usuki S, Yasunaga KI, Kamei Y, Nishinakamura R, Minami T, Fukuda T, Asakura A, Ono Y.
Nat Metab. 2022 Feb;4(2):180-189. doi: 10.1038/s42255-022-00533-9. Epub 2022 Feb 28.
PMID:35228746
Muscle Changes During Atrophy.
Dumitru A, Radu BM, Radu M, Cretoiu SM.
Adv Exp Med Biol. 2018;1088:73-92. doi: 10.1007/978-981-13-1435-3_4.
PMID:30390248
Endoplasmic reticulum stress and unfolded protein response: Roles in skeletal muscle atrophy.
Ji Y, Jiang Q, Chen B, Chen X, Li A, Shen D, Shen Y, Liu H, Qian X, Yao X, Sun H.
Biochem Pharmacol. 2025 Apr;234:116799. doi: 10.1016/j.bcp.2025.116799. Epub 2025 Feb 12.
PMID:39952329
Laminin-11.
Miner JH, Patton BL.
Int J Biochem Cell Biol. 1999 Aug;31(8):811-6. doi: 10.1016/s1357-2725(99)00030-8.
PMID:10481268
Intestinal pseudo-obstruction.
Moss AA, Goldberg HI.
CRC Crit Rev Radiol Sci. 1972;3(3):363-87.
PMID:4146635
Analysis of human urinary extracellular vesicles reveals disordered renal metabolism in myotonic dystrophy type 1.
Kumari P, Sullivan LM, Li Z, Parker Conquest E, Cornforth E, Jayakumar R, Hu N, Alexander Sizemore J, McKee BB, Kitchen RR, González-Pérez P, Linville C, Castro K, Gutierrez H, Samaan S, Townsend EL, Darras BT, Rutkove SB, Iannaccone ST, Clemens PR, Puwanant A, Das S, Wheeler TM.
Nat Commun. 2025 Mar 5;16(1):2158. doi: 10.1038/s41467-025-56479-5.
PMID:40044661
Increased Adenine Nucleotide Degradation in Skeletal Muscle Atrophy.
Miller SG, Hafen PS, Brault JJ.
Int J Mol Sci. 2019 Dec 21;21(1):88. doi: 10.3390/ijms21010088.
PMID:31877712
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