Spinal Muscular Atrophy Treatment in Patients Identified by Newborn Screening-A Systematic Review.
Aragon-Gawinska K, Mouraux C, Dangouloff T, Servais L.
Genes (Basel). 2023 Jun 29;14(7):1377. doi: 10.3390/genes14071377.
PMID:37510282
Spinal Muscular Atrophy: An Evolving Scenario through New Perspectives in Diagnosis and Advances in Therapies.
Angilletta I, Ferrante R, Giansante R, Lombardi L, Babore A, Dell'Elice A, Alessandrelli E, Notarangelo S, Ranaudo M, Palmarini C, De Laurenzi V, Stuppia L, Rossi C.
Int J Mol Sci. 2023 Oct 3;24(19):14873. doi: 10.3390/ijms241914873.
PMID:37834320
Spinal Muscular Atrophy: Current Medications and Re-purposed Drugs.
Basak S, Biswas N, Gill J, Ashili S.
Cell Mol Neurobiol. 2024 Nov 8;44(1):75. doi: 10.1007/s10571-024-01511-3.
PMID:39514016
Spinal Muscular Atrophy: A (Now) Treatable Neurodegenerative Disease.