Advances and limitations for the treatment of spinal muscular atrophy.
Day JW, Howell K, Place A, Long K, Rossello J, Kertesz N, Nomikos G.
BMC Pediatr. 2022 Nov 3;22(1):632. doi: 10.1186/s12887-022-03671-x.
PMID:36329412
Spinal Muscular Atrophy: An Evolving Scenario through New Perspectives in Diagnosis and Advances in Therapies.
Angilletta I, Ferrante R, Giansante R, Lombardi L, Babore A, Dell'Elice A, Alessandrelli E, Notarangelo S, Ranaudo M, Palmarini C, De Laurenzi V, Stuppia L, Rossi C.
Int J Mol Sci. 2023 Oct 3;24(19):14873. doi: 10.3390/ijms241914873.
PMID:37834320
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