Duchenne muscular dystrophy.
Duan D, Goemans N, Takeda S, Mercuri E, Aartsma-Rus A.
Nat Rev Dis Primers. 2021 Feb 18;7(1):13. doi: 10.1038/s41572-021-00248-3.
Therapeutic Strategies for Duchenne Muscular Dystrophy: An Update.
Sun C, Shen L, Zhang Z, Xie X.
Genes (Basel). 2020 Jul 23;11(8):837. doi: 10.3390/genes11080837.
Diagnosis and management of Duchenne muscular dystrophy, part 2: respiratory, cardiac, bone health, and orthopaedic management.
Birnkrant DJ, Bushby K, Bann CM, Alman BA, Apkon SD, Blackwell A, Case LE, Cripe L, Hadjiyannakis S, Olson AK, Sheehan DW, Bolen J, Weber DR, Ward LM; DMD Care Considerations Working Group.
Lancet Neurol. 2018 Apr;17(4):347-361. doi: 10.1016/S1474-4422(18)30025-5. Epub 2018 Feb 3.
CRISPR-Cas9 Gene Therapy for Duchenne Muscular Dystrophy.
Happi Mbakam C, Lamothe G, Tremblay G, Tremblay JP.
Neurotherapeutics. 2022 Apr;19(3):931-941. doi: 10.1007/s13311-022-01197-9. Epub 2022 Feb 14.
Duchenne Muscular Dystrophy: From Diagnosis to Therapy.
Falzarano MS, Scotton C, Passarelli C, Ferlini A.
Molecules. 2015 Oct 7;20(10):18168-84. doi: 10.3390/molecules201018168.
Duchenne muscular dystrophy.
Yiu EM, Kornberg AJ.
J Paediatr Child Health. 2015 Aug;51(8):759-64. doi: 10.1111/jpc.12868. Epub 2015 Mar 9.
Exercise Training in Duchenne Muscular Dystrophy: A Systematic Review and Meta-Analysis.
Hammer S, Toussaint M, Vollsæter M, Nesbjørg Tvedt M, Drange Røksund O, Reychler G, Lund H, Andersen T.
J Rehabil Med. 2022 Jan 11;54:jrm00250. doi: 10.2340/jrm.v53.985.
[Update on Duchenne muscular dystrophy].
Leiva-Cepas F, Montaño Martínez A, López-López I.
Semergen. 2021 Oct;47(7):472-481. doi: 10.1016/j.semerg.2021.06.008. Epub 2021 Aug 18.
Therapeutic developments for Duchenne muscular dystrophy.
Verhaart IEC, Aartsma-Rus A.
Nat Rev Neurol. 2019 Jul;15(7):373-386. doi: 10.1038/s41582-019-0203-3.
The importance of genetic diagnosis for Duchenne muscular dystrophy.
Aartsma-Rus A, Ginjaar IB, Bushby K.
J Med Genet. 2016 Mar;53(3):145-51. doi: 10.1136/jmedgenet-2015-103387. Epub 2016 Jan 11.
