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Targeting Wolman Disease and Cholesteryl Ester Storage Disease: Disease Pathogenesis and Therapeutic Development.
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Sebelipase alfa for treating Wolman disease.
[No authors listed]
London: National Institute for Health and Care Excellence (NICE); 2024 Jan 10.
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Modeling Steatohepatitis in Humans with Pluripotent Stem Cell-Derived Organoids.
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Wolman's disease presenting with secondary hemophagocytic lymphohistiocytosis: a case report from Saudi Arabia and literature review.
Alabbas F, Elyamany G, Alanzi T, Ali TB, Albatniji F, Alfaraidi H.
BMC Pediatr. 2021 Feb 10;21(1):72. doi: 10.1186/s12887-021-02541-2.
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Recent insights into lysosomal acid lipase deficiency.
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